Expanded Access News & Webinars

Suma Babu, MBBS, MPH of Massachusetts General Hospital was joined by Michael Hayden, MBChB, PhD, Chief Executive Officer of Prilenia Therapeutics, to discuss news and updates about Pridopidine, the investigational product studied in Regimen D of the HEALEY ALS Platform Trial, and answer questions from the audience. 
Watch Recording 

January 25, 2024: CNM-Au8 Update and Q&A with Clene Nanomedicine
Sabrina Paganoni, MD, PhD of Massachusetts General Hospital was joined by Jinsy Andrews, MD, MSc of Columbia University and Karen Ho, PhD from Clene Nanomedicine to discuss news and updates about CNM-Au8, the investigational product studied in Regimen C of the HEALEY ALS Platform Trial, and answer questions from the audience.
Watch Recording

May 14, 2021: NEALS 2021 ALS Drug Development Webinar Series: Site Considerations
Drs. Suma Babu and Katherine Nicholson discuss some of the issues faced by sites in a clinical trial including the specific steps and resources a site needs to open and run a clinical trial and an expanded access program.
Watch Recording

April 18, 2024: Expanded Access and Patient Navigation

Sabrina Paganoni, MD, PhD of Massachusetts General Hospital was joined by Patient Navigators Catherine Small and Allison Bulat, along with Research Access Nurse Judi Carey, to discuss Expanded Access and answer questions from the audience. This week, we provided an overview of four newly launched webpages and highlighted online resources to learn more about Expanded Access Protocols (EAPs). 
Watch Recording | Download Slides

March 14, 2024: EAP Discussion with Dr. Jinsy Andrews
Sabrina Paganoni, MD, PhD, of Massachusetts General Hospital was joined by Jinsy Andrews, MD, Msc, FAAN, FANA, of Columbia University to discuss news and updates about Expanded Access in the field of ALS research. Dr. Andrews provided an overview about Expanded Access, outlined plans for Clene Nanomedicine's upcoming NIH-funded EAP for CNM-Au8, and answered questions from the audience. 
Watch Recording

February 8, 2024: EAP Discussion with Dr. Rick Bedlack and Gwen Petersen 
Sabrina Paganoni, MD, PhD, of Massachusetts General Hospital was joined by Richard Bedlack, MD, PhD, MS of Duke University and Patient Advocate Gwen Petersen to discuss progress and ongoing initiatives for Expanded Access in the field of ALS research. The guest speakers shared their experiences advocating for EAPs and answered questions from the audience.
Watch Recording

January 18, 2024: Pridopidine Update and Q&A with Prilenia Therapeutics
Sabrina Paganoni, MD, PhD of Massachusetts General Hospital was joined by Michael Hayden, MBChB, PhD, Chief Executive Officer of Prilenia Therapeutics, to discuss news and updates about Pridopidine, the investigational product studied in Regimen D of the HEALEY ALS Platform Trial, and answer questions from the audience.
Watch Recording

January 11, 2024: Expanded Access Discussion with Amy Tsou, MD, MSc of the NIH
Sabrina Paganoni, MD, PhD, and Suma Babu, MBBS, MPH, of Massachusetts General Hospital were joined by Amy Tsou, MD, MSc and other guest speakers from the National Institute of Neurological Disorders and Stroke (NINDS) to discuss news and updates about Expanded Access in the field of ALS research. Dr. Tsou provided an overview of ongoing Expanded Access initiatives and answered questions from the audience. 
Watch Recording